Aplastic Anemia
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CLINICAL_TRIALS trial_result · 2026-08-10Clinical Trial Results: A Phase II Dose-escalation Study Characterizing the PK of Eltrombopag in Pediatric Patients With Previously Untreated or Relapsed Severe Aplastic Anemia or Recurrent Aplastic Anemia [Phase 2]
Phase II dose-escalation study evaluating the pharmacokinetics of eltrombopag in pediatric patients with severe or recurrent aplastic anemia…
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CLINICAL_TRIALS trial_result · 2026-04-24Clinical Trial Update: Randomized Study In Severe Aplastic Anemia Patients Receiving Atg, Cyclosporin A, With Or Without G-CSF (SAA-G-CSF) [Phase 3]
Phase 3 randomized trial evaluating ATG with or without G-CSF in severe aplastic anemia was terminated.
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CLINICAL_TRIALS trial_result · 2026-04-24Clinical Trial Update: hATG+CsA vs hATG+CsA+Eltrombopag for SAA [Phase 3]
A Phase 3 clinical trial comparing horse anti-thymocyte globulin plus cyclosporine with and without eltrombopag for severe aplastic anemia h…
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CLINICAL_TRIALS trial_result · 2026-04-14Clinical Trial Update: Cancer in Inherited Bone Marrow Failure Syndromes
This clinical trial is currently recruiting to study cancer in inherited bone marrow failure syndromes, including Diamond Blackfan Anemia, D…
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CLINICAL_TRIALS trial_result · 2026-04-13Clinical Trial Update: CsA+EPAG/HPAG+Romiplostim N01 in the Treatment of Newly-diagnosed SAA/TD-NSAA [Phase 2]
This Phase 2 clinical trial update describes a regimen of cyclosporine with EPAG/HPAG and romiplostim for newly diagnosed severe aplastic an…
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CLINICAL_TRIALS trial_result · 2026-04-06Clinical Trial Update: Geriatric Optimization Plan to Improve Survival in Older Adult Allogeneic Hematopoietic Cell Transplant Candidates, OTIS Study [NA]
Completed clinical trial evaluating a geriatric optimization plan to improve survival in older adults undergoing allogeneic hematopoietic ce…
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CLINICAL_TRIALS trial_result · 2026-03-27Clinical Trial Update: Radiation- and Alkylator-free Bone Marrow Transplantation Regimen for Patients With Dyskeratosis Congenita [Phase 2]
Phase 2 clinical trial update describing a radiation- and alkylator-free bone marrow transplantation regimen for patients with Dyskeratosis …
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CLINICAL_TRIALS trial_result · 2026-02-19Clinical Trial Update: A Study of the Safety and Effectiveness of Eltrombopag in Combination With Immunosuppressive Therapy (IST) in Korean Pediatric Patients With Treatment Naïve Severe Aplastic Anemia
This completed pediatric trial in Korea studied eltrombopag in combination with immunosuppressive therapy for treatment-naïve severe aplasti…
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CLINICAL_TRIALS trial_result · 2026-02-11Clinical Trial Update: A Single-Arm Phase 2 Study With Optimized Standard Protocol for Severe Aplastic Anemia [Phase 2]
Completed Phase 2 trial evaluating an optimized standard protocol for severe aplastic anemia.
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CLINICAL_TRIALS trial_result · 2026-02-11Clinical Trial Update: Efficacy and Safety of Low-dose Decitabine in Refractory Aplastic Anemia [Phase 2]
A Phase 2 trial evaluating low-dose decitabine for refractory aplastic anemia has been terminated.
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CLINICAL_TRIALS trial_result · 2026-02-11Clinical Trial Update: In Vitro Effect Study of Interleukin-2 Muteins on Regulatory T Cells of Patients With Different Autoimmune, Allo-immune or Inflammatory Diseases [NA]
A completed clinical trial update reporting an in vitro study of interleukin-2 muteins on regulatory T cells in patients with autoimmune, al…
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CLINICAL_TRIALS trial_result · 2026-01-16Clinical Trial Update: Sirolimus (Rapamune ) for Relapse Prevention in People With Severe Aplastic Anemia Responsive to Immunosuppressive Therapy [Phase 2]
Phase 2 trial evaluating sirolimus (Rapamune) for relapse prevention in people with severe aplastic anemia who previously responded to immun…
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CLINICAL_TRIALS trial_result · 2026-01-15Clinical Trial Update: A Study of Romiplostim N01 Plus IST vs. Placebo Plus IST for Treatment-Naive Severe Aplastic Anemia [Phase 3]
Phase 3 study comparing Romiplostim N01 plus immunosuppressive therapy versus placebo plus IST in treatment-naive severe aplastic anemia. Th…
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CLINICAL_TRIALS trial_result · 2026-01-05Clinical Trial Update: Clinical Transplant-Related Long-term Outcomes of Alternative Donor Allogeneic Transplantation (BMT CTN 1702) [NA]
A completed clinical trial update reporting long-term outcomes of alternative donor allogeneic transplantation across multiple hematologic d…
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CLINICAL_TRIALS trial_result · 2025-12-30Clinical Trial Update: Tolerance of Teeth Brushing During Prolonged Aplasia [Phase 3]
Phase 3 trial completed evaluating tolerability of teeth brushing in patients with prolonged aplasia.
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CLINICAL_TRIALS trial_result · 2025-12-23Clinical Trial Update: Impact of Supportive Care on the Experience of Hospitalization of Patients Staying in the Protected Area of the Department of Blood Diseases [NA]
Completed clinical trial assessing the impact of supportive care on the hospitalization experience for patients with acute leukemia undergoi…
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CLINICAL_TRIALS trial_result · 2025-10-30Clinical Trial Update: Haploidentical Hematopoietic Cell Transplantation Using TCR Alpha/Beta and CD19 Depletion [NA]
Clinical trial update from Baylor College of Medicine reports results for haploidentical hematopoietic cell transplantation using TCR alpha/…
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CLINICAL_TRIALS trial_result · 2025-10-24Clinical Trial Update: REGN7257 in Adult Patients With Severe Aplastic Anemia That Is Refractory to or Relapsed on Immunosuppressive Therapy [Phase 1]
Phase 1 trial of REGN7257 in adults with severe aplastic anemia refractory to or relapsed on immunosuppressive therapy has been terminated.
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CLINICAL_TRIALS trial_result · 2025-10-23Clinical Trial Update: Methadone as an Alternative Treatment for Children Underdoing HSCT [Phase 3]
Phase 3 trial evaluating methadone as an alternative treatment for children undergoing hematopoietic stem cell transplantation; the study is…
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CLINICAL_TRIALS trial_result · 2025-09-22Clinical Trial Update: Modified Transplantation Regimen and aGVHD Prophylaxis for Severe Aplastic Anemia in the Setting of Allogeneic HSCT.
This clinical trial reports results on a modified transplantation regimen and acute graft-versus-host disease prophylaxis for patients with …
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CLINICAL_TRIALS trial_result · 2025-09-16Clinical Trial Update: Efficacy and Safety in Transfusion Independent Non-severe Aplastic Anemia [Phase 2]
Phase 2 trial results evaluating efficacy and safety in transfusion-independent non-severe aplastic anemia.
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CLINICAL_TRIALS trial_result · 2025-07-22Clinical Trial Update: Efficacy and Safety of UCBT With TMI -Based Conditioning Regimen for Adults With Refractory/Relapsed Aplastic Anemia [Phase 2]
Phase 2 clinical trial evaluating Umbilical Cord Blood Transplant with a TMI-based conditioning regimen for adults with refractory or relaps…
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CLINICAL_TRIALS trial_result · 2025-07-17Clinical Trial Update: Combination of Eltrombopag With Immunosuppressive Therapy in East-Asian Patients With Severe Aplastic Anemia [Phase 2]
A Phase 2 trial evaluating eltrombopag in combination with immunosuppressive therapy for East-Asian patients with severe aplastic anemia has…
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CLINICAL_TRIALS trial_result · 2025-06-10Clinical Trial Update: Efficacy and Safety of Eltrombopag + CSA in Patients With Moderate Aplastic Anemia (EMAA) [Phase 2, Phase 3]
This update reports on the efficacy and safety of combining eltrombopag with cyclosporine A in patients with moderate aplastic anemia from P…
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CLINICAL_TRIALS trial_result · 2025-05-11Clinical Trial Update: Unrelated Donor Transplant Versus Immune Therapy in Pediatric Severe Aplastic Anemia [NA]
This clinical trial has completed and reports results comparing unrelated donor transplant versus immune therapy in pediatric severe aplasti…