Adenylosuccinate Synthase Deficiency

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CLINICAL_TRIALS research · 2026-04-07
Clinical Trial Update: A Phase 1b Study of Adenylosuccinic Acid (ASA-001) for Adenylosuccinate Synthase 1 (ADSS1) Deficient Myopathy. [Phase 1]
This clinical trial update describes a Phase 1b study of Adenylosuccinic acid (ASA-001) for Adenylosuccinate synthase 1 (ADSS1) deficient my…