Clinical Trial Update: A Phase 1b Study of Adenylosuccinic Acid (ASA-001) for Adenylosuccinate Synthase 1 (ADSS1) Deficient Myopathy. [Phase 1]

View source ↗

Summary

This clinical trial update describes a Phase 1b study of Adenylosuccinic acid (ASA-001) for Adenylosuccinate synthase 1 (ADSS1) deficient myopathy, with enrollm…

Upgrade for the full analysis, importance score, and drug timeline.

Diseases / indications

• Adenylosuccinate Synthase Deficiency

Drugs mentioned

• Adenylosuccinic acid (ASA-001) (Adenylosuccinic acid)

Snippet

Sponsor: Cure ADSSL1 | Conditions: Adenylosuccinate Synthase 1 Deficient Myopathy | Phase 1 | Status: ENROLLING_BY_INVITATION