Adenosine Deaminase Severe Combined Immunodeficiency
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CLINICAL_TRIALS research · 2026-04-07Clinical Trial Update: Gene Therapy for Adenosine Deaminase Severe Combined Immune Deficiency Using Peripheral Blood and EFS ADA Vector [Phase 1, Phase 2]
A Phase 1/2 clinical trial evaluating an ADA gene therapy vector delivered via peripheral blood for Adenosine Deaminase Severe Combined Immu…
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CLINICAL_TRIALS research · 2025-09-09Clinical Trial Update: Gene Therapy for ADA-SCID Using an Improved Lentiviral Vector (Ivlv-ADA) [NA]
This clinical trial update discusses a gene therapy approach for ADA-SCID using an improved lentiviral vector called Ivlv-ADA, being develop…
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CLINICAL_TRIALS trial_result · 2024-11-15Clinical Trial Update: Registry Study of Revcovi Treatment in Patients With ADA-SCID
Registry study evaluating Revcovi for ADA-SCID has completed. Results have been posted.