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CLINICAL_TRIALS research · 2026-04-07

Clinical Trial Update: Gene Therapy for Adenosine Deaminase Severe Combined Immune Deficiency Using Peripheral Blood and EFS ADA Vector [Phase 1, Phase 2]

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Summary

A Phase 1/2 clinical trial evaluating an ADA gene therapy vector delivered via peripheral blood for Adenosine Deaminase Severe Combined Immunodeficiency, sponso…

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Diseases / indications

Drugs mentioned

  • EFS ADA Vector (ADA gene therapy vector)

Snippet

Sponsor: University of California, Los Angeles | Conditions: Adenosine Deaminase Severe Combined Immune Deficiency | Phase 1, Phase 2 | Status: RECRUITING