Adenosine Deaminase Deficiency
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS trial_result · 2021-09-16Clinical Trial Update: Lentiviral (LV) Gene Therapy for Adenosine Deaminase (ADA) Deficiency [Phase 1, Phase 2]
Phase 1/2 lentiviral gene therapy trial for ADA deficiency/SCID completed with results posted in 2021.
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CLINICAL_TRIALS trial_result · 2020-04-16Clinical Trial Update: EZN-2279 in Patients With ADA-SCID [Phase 3]
Phase 3 trial update for EZN-2279 in ADA-SCID has completed; results posted in 2020.
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CLINICAL_TRIALS trial_result · 2015-09-14Clinical Trial Update: Gene Therapy ADA Deficiency [Phase 1, Phase 2]
A completed Phase 1/2 gene therapy trial for Adenosine Deaminase Deficiency sponsored by Great Ormond Street Hospital for Children NHS Found…