Clinical Trial Update: Gene Therapy ADA Deficiency [Phase 1, Phase 2]

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Summary

A completed Phase 1/2 gene therapy trial for Adenosine Deaminase Deficiency sponsored by Great Ormond Street Hospital for Children NHS Foundation Trust.

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Diseases / indications

• Adenosine Deaminase Deficiency

Drugs mentioned

• ADA gene therapy (experimental)

Snippet

Sponsor: Great Ormond Street Hospital for Children NHS Foundation Trust | Conditions: Adenosine Deaminase Deficiency | Phase 1, Phase 2 | Status: COMPLETED