Acid Maltase Deficiency Disease
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS trial_result · 2022-08-26Clinical Trial Update: Growth and Development Study of Alglucosidase Alfa [Phase 4]
A Phase 4 clinical trial update for alglucosidase alfa investigating growth and development in Pompe disease, with results posted after comp…
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CLINICAL_TRIALS trial_result · 2014-02-05Clinical Trial Update: A Study of the Safety and Pharmacokinetics of rhGAA in Siblings With Glycogen Storage Disease Type II [Phase 2]
Phase 2 study evaluating the safety and pharmacokinetics of recombinant human acid alpha-glucosidase (rhGAA) in siblings with glycogen stora…