CLINICAL_TRIALS
research
· 2024-11-13
Clinical Trial Update: Natural History Study in Pediatric Patients With MYBPC3 Mutation-associated Cardiomyopathy
Summary
Pediatric natural history study investigating MYBPC3 mutation-associated cardiomyopathy, currently recruiting to characterize disease course.
Upgrade for the full analysis, importance score, and drug timeline.
Diseases / indications
Snippet
Sponsor: Tenaya Therapeutics | Conditions: Cardiomyopathy | Status: RECRUITING