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CLINICAL_TRIALS trial_result · 2026-04-17

Clinical Trial Update: Glycerol Phenylbutyrate Corrector Therapy For CF (Cystic Fibrosis) [Phase 1, Phase 2]

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Summary

Phase 1/2 clinical trial of glycerol phenylbutyrate as a potential cystic fibrosis therapy was terminated; results have been posted.

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Diseases / indications

Drugs mentioned

  • Glycerol phenylbutyrate (glycerol phenylbutyrate)

Snippet

Sponsor: National Jewish Health | Conditions: Cystic Fibrosis | Phase 1, Phase 2 | Status: TERMINATED | Results posted: 2026-04-17