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CLINICAL_TRIALS trial_result · 2025-11-20

Clinical Trial Update: Effect of Miglustat on the Nasal Potential Difference in Patients With Cystic Fibrosis Homozygous for the F508del Mutation [Phase 2, Phase 3]

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Summary

This update reports the completion of a Phase 2/3 trial assessing miglustat's effect on nasal potential difference in cystic fibrosis patients homozygous for th…

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Diseases / indications

Drugs mentioned

  • Miglustat (miglustat)

Snippet

Sponsor: Assistance Publique - Hôpitaux de Paris | Conditions: Cystic Fibrosis | Phase 2, Phase 3 | Status: COMPLETED