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CLINICAL_TRIALS research · 2026-01-21

Clinical Trial Update: Study to Evaluate Elexacaftor/Tezacaftor/Ivacaftor (ELX/TEZ/IVA) Long-term Safety and Efficacy in Subjects Without F508del [Phase 3]

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Summary

Phase 3 long-term safety and efficacy study of elexacaftor/tezacaftor/ivacaftor in cystic fibrosis patients without the F508del mutation; the trial is currently…

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Diseases / indications

Drugs mentioned

  • TRIKAFTA (ELEXACAFTOR, TEZACAFTOR, AND IVACAFTOR)

Snippet

Sponsor: Vertex Pharmaceuticals Incorporated | Conditions: Cystic Fibrosis | Phase 3 | Status: ACTIVE_NOT_RECRUITING