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CLINICAL_TRIALS research · 2026-02-20

Clinical Trial Update: Study to Evaluate Safety, Tolerability and Efficacy of Inclisiran in Children With Homozygous Familial Hypercholesterolemia [Phase 3]

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Summary

A Phase 3 clinical trial is evaluating the safety, tolerability, and efficacy of Inclisiran in children with homozygous familial hypercholesterolemia. The study…

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Diseases / indications

Drugs mentioned

  • Inclisiran (inclisiran)

Snippet

Sponsor: Novartis Pharmaceuticals | Conditions: Familial Hypercholesterolemia - Homozygous | Phase 3 | Status: RECRUITING