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CLINICAL_TRIALS trial_result · 2026-02-23

Clinical Trial Update: A Study of DB-OTO, an Adeno-Associated Virus (AAV) Based Gene Therapy, in Children/Infants With Hearing Loss Due to Otoferlin Mutations [Phase 1, Phase 2]

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Summary

Regeneron's DB-OTO, an AAV-based gene therapy, is being evaluated in Phase 1/2 for congenital hearing loss due to biallelic OTOF mutations and is currently recr…

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Diseases / indications

Drugs mentioned

  • DB-OTO

Snippet

Sponsor: Regeneron Pharmaceuticals | Conditions: Congenital Hearing Loss Secondary to Biallelic Mutations of the Otoferlin Gene (OTOF) | Phase 1, Phase 2 | Status: RECRUITING