CLINICAL_TRIALS
trial_result
· 2025-05-02
Clinical Trial Update: Study of Gene Therapy Using a Lentiviral Vector to Treat X-linked Chronic Granulomatous Disease [Phase 1, Phase 2]
Summary
A Phase 1/2 clinical trial using a lentiviral vector gene therapy to treat X-linked chronic granulomatous disease has completed.
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Drugs mentioned
Snippet
Sponsor: University of California, Los Angeles | Conditions: Granulomatous Disease, Chronic, X-linked | Phase 1, Phase 2 | Status: COMPLETED