X-linked Retinitis Pigmentosa
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CLINICAL_TRIALS trial_result · 2026-07-06Clinical Trial Update: Long-term Safety and Efficacy Follow-up of BIIB111 for the Treatment of Choroideremia and BIIB112 for the Treatment of X-Linked Retinitis Pigmentosa [Phase 3]
Phase 3 long-term safety and efficacy follow-up study for BIIB111 in choroideremia and BIIB112 in X-linked retinitis pigmentosa has complete…
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CLINICAL_TRIALS trial_result · 2026-06-05Clinical Trial Update: A Study of AAV5-hRKp.RPGR for the Treatment of Japanese Participants With X-linked Retinitis Pigmentosa [Phase 3]
Phase 3 trial update for AAV5-hRKp.RPGR in Japanese participants with X-linked Retinitis Pigmentosa (inactive/recruiting status noted).
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CLINICAL_TRIALS trial_result · 2026-06-05Clinical Trial Update: Follow-up Gene Therapy Trial for the Treatment of X-linked Retinitis Pigmentosa Associated With Variants in the RPGR Gene [Phase 3]
Phase 3 follow-up trial update for a gene therapy targeting X-linked Retinitis Pigmentosa caused by RPGR variants; trial status is active bu…
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CLINICAL_TRIALS trial_result · 2026-04-13Clinical Trial Update: A Study of AAV5-hRKp.RPGR for the Treatment of Japanese Participants With X-linked Retinitis Pigmentosa [Phase 3]
Phase 3 study evaluating AAV5-hRKp.RPGR for X-linked Retinitis Pigmentosa in Japanese participants is active but not recruiting.
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CLINICAL_TRIALS research · 2026-04-13Clinical Trial Update: Follow-up Gene Therapy Trial for the Treatment of X-linked Retinitis Pigmentosa Associated With Variants in the RPGR Gene [Phase 3]
Phase 3 follow-up trial update for a gene therapy targeting X-linked retinitis pigmentosa caused by RPGR variants; study status is active bu…
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CLINICAL_TRIALS research · 2026-04-13Clinical Trial Update: A Follow-on Study for Second-Eye Treatment for Participants Previously Treated With Gene Therapy for X-Linked Retinitis Pigmentosa (XLRP) [Phase 2]
This clinical trial update describes a Phase 2 follow-on study evaluating a second-eye treatment in participants with X-linked retinitis pig…
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CLINICAL_TRIALS trial_result · 2026-04-07Clinical Trial Update: A Clinical Trial Evaluating the Safety and Efficacy of a Single Subretinal Injection of AGTC-501 in Participants With XLRP [Phase 2, Phase 3]
A Phase 2/3 clinical trial update for AGTC-501 in X-linked Retinitis Pigmentosa, with a subretinal injection approach, showing the study is …
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CLINICAL_TRIALS trial_result · 2026-03-16Clinical Trial Update: Gene Therapy Trial for the Treatment of X-linked Retinitis Pigmentosa Associated With Variants in the RPGR Gene [Phase 3]
A Phase 3 gene therapy trial for X-linked retinitis pigmentosa caused by RPGR variants has completed, with Janssen providing the status upda…
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CLINICAL_TRIALS trial_result · 2026-02-19Clinical Trial Update: A Phase 2 Open-label Study to Evaluate the Safety of Laruparetigene Zovaparvovec Administered Bilaterally in Male Participants With X-Linked Retinitis Pigmentosa [Phase 2]
This is a Phase 2 open-label study to evaluate the safety of Laruparetigene Zovaparvovec administered bilaterally in male participants with …
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CLINICAL_TRIALS trial_result · 2026-01-21Clinical Trial Update: Long-term Follow-up Gene Therapy Study for RPGR- XLRP
This entry reports a completed long-term follow-up of a gene therapy trial for RPGR-XLRP (X-Linked Retinitis Pigmentosa) sponsored by Jansse…
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CLINICAL_TRIALS research · 2025-06-12Clinical Trial Update: Long-term Safety and Efficacy Follow-up of BIIB111 for the Treatment of Choroideremia and BIIB112 for the Treatment of X-Linked Retinitis Pigmentosa [Phase 3]
This clinical trial update outlines long-term safety and efficacy follow-up for BIIB111 in choroideremia and BIIB112 for X-linked retinitis …
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CLINICAL_TRIALS research · 2025-05-21Clinical Trial Update: InsightRP2 Registry
InsightRP2 Registry is a clinical trial registry monitoring RP2-associated retinitis pigmentosa and X-linked retinitis pigmentosa, currently…
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CLINICAL_TRIALS trial_result · 2025-04-25Clinical Trial Update: An Observational Study of Japanese Participants With X-linked Retinitis Pigmentosa
An observational study completed in Japanese participants with X-linked retinitis pigmentosa, sponsored by Janssen Pharmaceutical K.K., repo…
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CLINICAL_TRIALS trial_result · 2025-03-21Clinical Trial Update: 4D-125 in Patients With X-Linked Retinitis Pigmentosa (XLRP) [Phase 1, Phase 2]
This clinical trial update indicates that 4D-125 is being studied in Phase 1/2 for X-Linked Retinitis Pigmentosa and the study is currently …
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CLINICAL_TRIALS trial_result · 2025-01-08Clinical Trial Update: Gene Therapy for X-linked Retinitis Pigmentosa (XLRP) - Retinitis Pigmentosa GTPase Regulator (RPGR) [Phase 1, Phase 2]
A phase 1/2 gene therapy trial targeting RPGR in X-linked Retinitis Pigmentosa has completed and posted results in January 2025.
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CLINICAL_TRIALS research · 2024-10-30Clinical Trial Update: A Study Comparing Two Doses of AGTC-501 in Male Participants With X-linked Retinitis Pigmentosa Caused by RPGR Mutations (DAWN) [Phase 2]
Phase 2 study comparing two doses of AGTC-501 in male participants with X-linked retinitis pigmentosa caused by RPGR mutations; enrollment i…
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CLINICAL_TRIALS research · 2024-08-12Clinical Trial Update: A Study Comparing Two Doses of AGTC-501 in Male Subjects With X-linked Retinitis Pigmentosa Caused by RPGR Mutations (SKYLINE) [Phase 2]
This clinical trial update describes a Phase 2 study (SKYLINE) evaluating two doses of AGTC-501 in male participants with X-linked retinitis…
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CLINICAL_TRIALS research · 2024-07-09Clinical Trial Update: Gene Therapy for RPGR Gene Mutation-associated X-linked Retinitis Pigmentosa [Phase 1, Phase 2]
This clinical trial update describes an investigational RPGR gene therapy for X-linked retinitis pigmentosa, currently in Phase 1/2 and recr…
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CLINICAL_TRIALS trial_result · 2024-06-20Clinical Trial Update: Natural History Study of Patients With X-linked Retinal Dystrophy Associated With Mutations in Retinitis Pigmentosa GTPase Regulator (RPGR)
This clinical trial update reports the completion of a natural history study in patients with X-linked retinitis pigmentosa associated with …
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CLINICAL_TRIALS trial_result · 2024-05-20Clinical Trial Update: Safety and Efficacy of rAAV2tYF-GRK1-RPGR in Subjects With X-linked Retinitis Pigmentosa Caused by RPGR Mutations [Phase 1, Phase 2]
Phase 1/2 clinical trial update on the safety and efficacy of the gene therapy vector rAAV2tYF-GRK1-RPGR for X-linked retinitis pigmentosa d…
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CLINICAL_TRIALS trial_result · 2024-01-18Clinical Trial Update: A Clinical Trial of Retinal Gene Therapy for X-linked Retinitis Pigmentosa Using BIIB112 [Phase 1, Phase 2]
Phase 1/2 clinical trial update for BIIB112 retinal gene therapy in X-linked retinitis pigmentosa has completed with results posted.
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CLINICAL_TRIALS research · 2015-03-25Clinical Trial Update: Study of Docosahexaenoic Acid (DHA) Supplementation in Patients With X-Linked Retinitis Pigmentosa [NA]
This is a completed clinical trial studying Docosahexaenoic acid (DHA) supplementation in patients with X-linked retinitis pigmentosa. The s…
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CLINICAL_TRIALS trial_result · 2015-03-17Clinical Trial Update: DHA and X-Linked Retinitis Pigmentosa [Phase 2]
A Phase 2 trial evaluated docosahexaenoic acid (DHA) for X-linked retinitis pigmentosa; results were posted after the study completed.