Wolman Disease

• CLINICAL_TRIALS trial_result · 2024-05-09
  Clinical Trial Update: Breakfast for Young Women [NA]

  This clinical trial update notes the completion of a University of Aarhus–sponsored study titled 'Breakfast for Young Women,' which investig…

• CLINICAL_TRIALS trial_result · 2016-04-18
  Clinical Trial Update: Safety, Tolerability, Efficacy, Pharmacokinetics, and Pharmacodynamics of Sebelipase Alfa in Children With Growth Failure Due to Lysosomal Acid Lipase Deficiency [Phase 2, Phase 3]

  This clinical trial update reports Phase 2/3 results for Sebelipase alfa in children with growth failure due to lysosomal acid lipase defici…