Variegate Porphyria
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS trial_result · 2026-01-30Clinical Trial Update: Panhematin for Prevention of Acute Attacks of Porphyria [Phase 2]
Phase 2 study of Panhematin (hemin) to prevent acute attacks in porphyrias was terminated, with results posted on 2026-01-30.
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CLINICAL_TRIALS trial_result · 2025-04-27Clinical Trial Update: Study to Evaluate the Safety and Efficacy of Afamelanotide in Patients With Variegate Porphyria (VP) [Phase 2]
Phase 2 study evaluating the safety and efficacy of afamelanotide in patients with Variegate Porphyria has completed and posted results.
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CLINICAL_TRIALS research · 2025-04-18Clinical Trial Update: Acute Porphyria Biomarkers for Disease Activity
An ongoing clinical trial from The University of Texas Medical Branch evaluating biomarkers for disease activity in porphyrias. The study is…
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CLINICAL_TRIALS trial_result · 2020-02-11Clinical Trial Update: ENVISION: A Study to Evaluate the Efficacy and Safety of Givosiran (ALN-AS1) in Patients With Acute Hepatic Porphyrias (AHP) [Phase 3]
Phase 3 trial evaluating givosiran (ALN-AS1) for acute hepatic porphyrias has been completed with results posted.
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CLINICAL_TRIALS trial_result · 2019-01-25Clinical Trial Update: INSIGHT-AHP: A Study to Characterize the Prevalence of Acute Hepatic Porphyria (AHP) in Patients With Clinical Presentation and History Consistent With AHP
A terminated Alnylam-sponsored study (INSIGHT-AHP) sought to characterize the prevalence of acute hepatic porphyrias among patients with cli…
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