Vanishing White Matter Disease
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS research · 2026-02-09Clinical Trial Update: Longitudinal Study of Neurodegenerative Disorders
This clinical trial update describes a longitudinal study of several neurodegenerative and lysosomal storage disorders. The study is current…
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CLINICAL_TRIALS research · 2025-12-30Clinical Trial Update: Research Study for Single-Patient Treatment of Cree Leukoencephalopathy/Vanishing White Matter Disease [EARLY_Phase 1]
A single-patient, early-phase 1 treatment trial for Cree Leukoencephalopathy and Vanishing White Matter Disease is active but not recruiting…
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CLINICAL_TRIALS research · 2025-11-12Clinical Trial Update: An Open-Label Exploratory Study of Fosigotifator in Participants With Vanishing White Matter Disease [Phase 1, Phase 2]
Open-label exploratory study of Fosigotifator in participants with Vanishing White Matter Disease is in Phase 1/Phase 2 and currently recrui…