Usher Syndrome Type Ii
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS trial_result · 2024-07-12Clinical Trial Update: Study to Evaluate the Efficacy Safety and Tolerability of Ultevursen in Subjects With RP Due to Mutations in Exon 13 of the USH2A Gene (Sirius) [Phase 2, Phase 3]
The Sirius study evaluating Ultevursen for retinitis pigmentosa due to USH2A exon 13 mutations (Phase 2/3) was terminated, with results post…
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CLINICAL_TRIALS trial_result · 2023-01-20Clinical Trial Update: Study to Evaluate the Efficacy Safety and Tolerability of QR-421a in Subjects With RP Due to Mutations in Exon 13 of the USH2A Gene With Early to Moderate Vision Loss (Celeste) [Phase 2, Phase 3]
A Phase 2/3 study evaluating QR-421a for retinitis pigmentosa due to USH2A exon 13 mutations was terminated, with results posted in January …