Usher Syndrome Type
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CLINICAL_TRIALS trial_result · 2026-02-04Clinical Trial Update: Rate of Progression in USH2A-related Retinal Degeneration
This clinical trial update indicates a study on the rate of progression in USH2A-related retinal degeneration is active but not currently re…
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CLINICAL_TRIALS trial_result · 2024-09-19Clinical Trial Update: BF844 Safety and Pharmacokinetic Study in Healthy Volunteers [Phase 1]
Phase 1 safety and pharmacokinetic study of BF844 in healthy volunteers, sponsored by EyeXCel Pty. Ltd., with Usher syndrome type 3 listed a…
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CLINICAL_TRIALS trial_result · 2022-12-27Clinical Trial Update: An Open-Label Extension Study to Evaluate Safety & Tolerability of QR-421a in Subjects With Retinitis Pigmentosa [Phase 2]
A Phase 2 open-label extension study evaluating the safety and tolerability of QR-421a in retinitis pigmentosa and Usher syndrome type 2 was…
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CLINICAL_TRIALS trial_result · 2022-04-20Clinical Trial Update: Study to Evaluate Safety and Tolerability of QR-421a in Subjects With RP Due to Mutations in Exon 13 of the USH2A Gene [Phase 1, Phase 2]
Phase 1/2 trial evaluating safety and tolerability of QR-421a in retinitis pigmentosa due to USH2A exon 13 mutations has completed.