Urea Cycle Disorders Inborn
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CLINICAL_TRIALS research · 2026-04-15Clinical Trial Update: An Open-label Study to Investigate ECUR-506 in Male Babies Less Than 9 Months of Age With Neonatal Onset OTC Deficiency [Phase 1, Phase 2]
This clinical trial update describes an open-label Phase 1/2 study evaluating ECUR-506 in male infants under 9 months with neonatal-onset Or…