Urea Cycle Disorder
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS trial_result · 2025-10-06Clinical Trial Update: At Home Ammonia Monitoring of Inborn Errors of Ammonia Metabolism [NA]
Clinical trial update on at-home ammonia monitoring for individuals with inborn errors of ammonia metabolism; enrollment is by invitation.
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CLINICAL_TRIALS trial_result · 2025-07-20Clinical Trial Update: Hepatic Histopathology in Urea Cycle Disorders
This clinical trial update indicates the study on hepatic histopathology in urea cycle disorders is actively recruiting, including Ornithine…
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CLINICAL_TRIALS trial_result · 2024-05-29Clinical Trial Update: HepaStem Long-Term Safety Registry
This clinical trial update announces the termination of the HepaStem long-term safety registry and highlights conditions studied (urea cycle…
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CLINICAL_TRIALS trial_result · 2023-07-10Clinical Trial Update: Study of Glycerol Phenylbutyrate & Sodium Phenylbutyrate in Phenylbutyrate Naïve Patients With Urea Cycle Disorders (UCDs) [Phase 4]
This Phase 4 study evaluated glycerol phenylbutyrate and sodium phenylbutyrate in phenylbutyrate-naïve patients with urea cycle disorders; t…
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CLINICAL_TRIALS trial_result · 2023-02-10Clinical Trial Update: Chronic Liver Disease in Urea Cycle Disorders
A completed clinical trial assessing chronic liver disease in individuals with urea cycle disorders; results posted in 2023.
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CLINICAL_TRIALS trial_result · 2021-02-18Clinical Trial Update: Observational Study That Will Collect Information on Patients With Urea Cycle Disorders (UCDs)
An observational trial sponsored by Amgen to collect information on patients with urea cycle disorders; the study is terminated and results …
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CLINICAL_TRIALS trial_result · 2019-03-05Clinical Trial Update: A Study of the Safety, Efficacy and Pharmacokinetics of Glycerol Phenylbutyrate in Pediatric Subjects Under 2 Years of Age With Urea Cycle Disorders [Phase 4]
Phase 4 clinical trial update assessing safety, efficacy and pharmacokinetics of glycerol phenylbutyrate in pediatric subjects under 2 years…
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CLINICAL_TRIALS trial_result · 2015-05-29Clinical Trial Update: Neurologic Injuries in Adults With Urea Cycle Disorders
A completed clinical trial update reporting results on neurologic injuries in adults with urea cycle disorders, including ornithine transcar…
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CLINICAL_TRIALS trial_result · 2014-11-05Clinical Trial Update: Arginine and Buphenyl in Patients With Argininosuccinic Aciduria (ASA), a Urea Cycle Disorder [Phase 2]
Phase 2 clinical trial update on arginine and buphenyl for argininosuccinic aciduria, a urea cycle disorder; trial completed with results po…