Tuberous Sclerosis

• CLINICAL_TRIALS trial_result · 2025-05-18
  Clinical Trial Update: Reproductive Options in Inherited Skin Diseases

  A clinical trial update indicates a study on reproductive options for inherited skin diseases is ongoing at Maastricht University Medical Ce…

• CLINICAL_TRIALS trial_result · 2023-08-14
  Clinical Trial Update: Dose-Ranging Efficacy and Safety Study of Topical Rapamycin Cream for Facial Angiofibroma Associated With Tuberous Sclerosis Complex [Phase 2, Phase 3]

  Phase 2/3 dose-ranging study evaluating topical rapamycin cream for facial angiofibroma in tuberous sclerosis complex has completed with res…

• CLINICAL_TRIALS trial_result · 2023-04-04
  Clinical Trial Update: Adjunctive Ganaxolone Treatment (Part A) in TSC Followed by Long-term Treatment (Part B) [Phase 2]

  Phase 2 clinical trial on adjunctive ganaxolone for tuberous sclerosis complex (TSC) completed with long-term treatment data posted.

• CLINICAL_TRIALS trial_result · 2020-10-26
  Clinical Trial Update: Topical Rapamycin to Erase Angiofibromas in TSC [Phase 2]

  Phase 2 trial evaluating topical rapamycin to reduce facial angiofibromas in tuberous sclerosis complex completed with results posted.

• CLINICAL_TRIALS trial_result · 2019-02-20
  Clinical Trial Update: Long-term Trial of Topical Sirolimus to Angiofibroma in Patient With Tuberous Sclerosis Complex [Phase 3]

  This entry reports the long-term results of a Phase 3 trial of topical sirolimus for angiofibromas in patients with tuberous sclerosis compl…

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• CLINICAL_TRIALS trial_result · 2018-01-30
  Clinical Trial Update: A Study of Everolimus in the Treatment of Neurocognitive Problems in Tuberous Sclerosis [Phase 2]

  Phase 2 clinical trial evaluating everolimus for neurocognitive problems in tuberous sclerosis.

• CLINICAL_TRIALS trial_result · 2012-05-01
  Clinical Trial Update: Efficacy and Safety of Everolimus (RAD001) in Patients of All Ages With Subependymal Giant Cell Astrocytoma Associated With Tuberous Sclerosis Complex (TSC)(EXIST-1) [Phase 3]

  Phase 3 EXIST-1 trial evaluating everolimus for subependymal giant cell astrocytoma in tuberous sclerosis complex demonstrates efficacy and …