Transfusion-dependent Thalassemia
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS trial_result · 2025-03-03Clinical Trial Update: Hematopoietic Stem Cell Transplant for High Risk Hemoglobinopathies [NA]
A hematopoietic stem cell transplant trial for high-risk hemoglobinopathies has been terminated; the conditions studied include sickle cell …
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CLINICAL_TRIALS research · 2024-10-28Clinical Trial Update: Evaluation of Recombinant Humanized Anti-CD25 Monoclonal Antibody for Preventing Graft-versus-host Disease After Haploidentical/matched Unrelated Donor Hematopoietic Stem Cell Transplantation in Patients with Transfusion-dependent Thalassemia [Phase 2]
A Phase 2 clinical trial evaluating a recombinant humanized anti-CD25 monoclonal antibody to prevent graft-versus-host disease after haploid…
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CLINICAL_TRIALS trial_result · 2024-03-08Clinical Trial Update: Efficacy of Combination of Hdroxyurea and Thalidomide Over Either Hydroxyurea or Thalidomide Alone in the Treatment of Transfusion Dependent Thalassemia in Children: A Quasi-Randomised Clinical Trial [Phase 4]
A Phase 4 quasi-randomised trial evaluates the efficacy of combining hydroxyurea and thalidomide versus each agent alone in children with tr…
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CLINICAL_TRIALS trial_result · 2021-10-04Clinical Trial Update: Open-label, Multicenter Study Assessing Preference for Deferasirox Film-coated Tablet Compared to Dispersible Tablet [Phase 2]
Phase 2 open-label multicenter trial assessing patient preference for deferasirox film-coated tablet versus dispersible tablet in thalassemi…
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CLINICAL_TRIALS trial_result · 2021-04-28Clinical Trial Update: Efficacy and Safety of RBCs Derived From Mirasol-treated Whole Blood in Patients Requiring Chronic Transfusion (PRAISE) [NA]
Clinical trial update for RBCs derived from Mirasol-treated whole blood in transfusion-dependent thalassemia; study terminated with posted r…
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FDA approval · 2019-11-20FDA Approved: DEFERASIROX — Original Application (Dr. Reddy's Laboratories Inc)
FDA approved Dr. Reddy's Laboratories' original application for deferasirox, a generic iron chelator used to treat chronic iron overload in …
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FDA approval · 2019-07-25FDA Approved: FERRIPROX — Supplemental Application (Chiesi USA, Inc.)
The FDA approved a supplemental application for Ferriprox (deferiprone) submitted by Chiesi USA, Inc., updating/expanding the product's labe…
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CLINICAL_TRIALS withdrawal · 2017-04-20Clinical Trial Update: Deferasirox BID (Twice a Day) in Transfusion Dependent Thalassemia Patients With Inadequate Response to High Doses [Phase 2]
A Phase 2 trial of twice-daily deferasirox in transfusion-dependent thalassemia patients inadequately responding to high-dose therapy has be…
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CLINICAL_TRIALS withdrawal · 2017-04-20Clinical Trial Update: Effect of Deferasirox on Endocrine Complications in Subjects With Transfusion Dependent Thalassemia [Phase 4]
A Phase 4 trial evaluating whether deferasirox affects endocrine complications in patients with transfusion-dependent thalassemia was withdr…
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FDA approval ·FDA Approves First Gene Therapy for Young Children with Sickle Cell Disease
FDA approves Casgevy (exagamglogene autotemcel) as a gene therapy for young children aged 2 years and older with sickle cell disease and rec…