Thymidine Kinase Deficiency
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CLINICAL_TRIALS withdrawal · 2023-09-01Clinical Trial Update: A Study of the Efficacy and Safety of MT1621 in Thymidine Kinase 2 (TK2) Deficiency (Treatment naïve) [Phase 3]
A Phase 3 trial evaluating MT1621 for Thymidine Kinase 2 deficiency was withdrawn.