Thalassemia
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS trial_result · 2022-03-18Clinical Trial Update: Hydroxyurea Therapy: Optimizing Access in Pediatric Populations Everywhere [Phase 2]
Phase 2 trial update on hydroxyurea therapy aimed at optimizing access in pediatric patients; study terminated with results posted.
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CLINICAL_TRIALS trial_result · 2021-11-24Clinical Trial Update: Clinical Experience of Thalidomide in Thalassemic Patients [Phase 2, Phase 3]
Clinical trial update reporting experience with thalidomide in thalassemia patients (Phase 2 and Phase 3; completed).
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CLINICAL_TRIALS trial_result · 2021-11-18Clinical Trial Update: A Study to Determine the Efficacy and Safety of Luspatercept in Adults With Non Transfusion Dependent Beta (β)-Thalassemia [Phase 2]
Phase 2 trial assessing efficacy and safety of luspatercept in adults with non transfusion dependent beta-thalassemia has completed with res…
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CLINICAL_TRIALS trial_result · 2021-11-15Clinical Trial Update: A Study to Determine the Efficacy, Safety, Pharmacokinetics, and Pharmacodynamics of AG-348 in Adult Participants With Non-transfusion-dependent Thalassemia [Phase 2]
Phase 2 clinical trial evaluating the efficacy, safety, pharmacokinetics, and pharmacodynamics of AG-348 (mitapivat) in adults with non-tran…
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CLINICAL_TRIALS trial_result · 2021-08-12Clinical Trial Update: Combined Chelation Therapy in Patients With Transfusion Dependent Thalassemia and Iron Overload [Phase 2]
Phase 2 trial update on combined chelation therapy for transfusion-dependent thalassemia with iron overload; study completed with posted res…
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CLINICAL_TRIALS trial_result · 2021-02-02Clinical Trial Update: L-Glutamine Therapy for Sickle Cell Anemia [Phase 2]
Phase 2 clinical trial of L-Glutamine therapy for sickle cell anemia has been terminated; results posted in 2021.
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CLINICAL_TRIALS trial_result · 2021-01-29Clinical Trial Update: L-Glutamine Therapy for Sickle Cell Anemia and Sickle ß0 Thalassemia [Phase 2]
Phase 2 clinical trial of L-Glutamine therapy for sickle cell anemia and sickle beta-zero thalassemia completed with results posted.
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CLINICAL_TRIALS trial_result · 2020-05-01Clinical Trial Update: Allogeneic Stem Cell Transplantation, Severe Homzygous 0/+Thalassemia or Sever Variants of Beta 0/+ Thalassemia, THALLO [NA]
Clinical trial update for allogeneic stem cell transplantation in severe beta-thalassemia variants; the study is terminated with results pos…
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CLINICAL_TRIALS trial_result · 2019-06-26Clinical Trial Update: Allogeneic SCT of CordIn™, in Patients With Hemoglobinopathies [Phase 1, Phase 2]
Phase 1/2 clinical trial update for Allogeneic cord blood stem cell therapy CordIn in sickle cell disease and thalassemia; study status term…
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CLINICAL_TRIALS trial_result · 2019-01-22Clinical Trial Update: Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of ISIS 702843 Administered Subcutaneously to Healthy Volunteers [Phase 1]
This Phase 1 trial update reports on the safety, tolerability, pharmacokinetics, and pharmacodynamics of ISIS 702843 administered subcutaneo…
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CLINICAL_TRIALS trial_result · 2018-12-27Clinical Trial Update: Colla Corii Asini Treating Anemia in Pregnant Women With Thalassemia(Presenting the Syndrome of Blood Deficiency) [Phase 4]
A Phase 4 trial investigating Colla Corii Asini for treating anemia in pregnant women with thalassemia is reported as ongoing with unknown s…
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CLINICAL_TRIALS trial_result · 2018-10-11Clinical Trial Update: Sofosbuvir/Ledipasvir for Hepatitis C Genotype 1-6 in Patients With Transfusion-Dependent Thalassemia: An Open Label Trial [Phase 4]
Phase 4 open-label trial assessing Sofosbuvir/Ledipasvir for Hepatitis C in patients with transfusion-dependent thalassemia has completed.
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CLINICAL_TRIALS trial_result · 2018-08-06Clinical Trial Update: Allo-HCT MUD for Non-malignant Red Blood Cell (RBC) Disorders: Sickle Cell, Thal, and DBA: Reduced Intensity Conditioning, Co-tx MSCs [Phase 2]
Phase 2 trial evaluating allogeneic hematopoietic cell transplantation from matched unrelated donor with reduced-intensity conditioning and …
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CLINICAL_TRIALS trial_result · 2018-01-16Clinical Trial Update: Study on the Mechanism of Colla Corri Asini in the Treatment of Thalassemia Patients With Pregnancy Anemia [Phase 4]
Phase 4 trial update exploring the mechanism of Colla Corri Asini in treating thalassemia in pregnant patients.
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CLINICAL_TRIALS trial_result · 2017-10-20Clinical Trial Update: Reduced Intensity Transplant Conditioning Regimen for Severe Thalassemia [Phase 2]
Phase 2 trial evaluating a reduced-intensity transplant conditioning regimen for severe thalassemia has completed, with results posted in Oc…
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CLINICAL_TRIALS trial_result · 2017-07-02Clinical Trial Update: Oral Nifedipine to Treat Iron Overload [Phase 1]
A Phase 1 trial evaluating oral nifedipine for treating iron overload in thalassemia has completed.
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CLINICAL_TRIALS trial_result · 2017-06-29Clinical Trial Update: Amlodipine for Myocardial Iron in Thalassemia [Phase 2, Phase 3]
A phase 2/3 clinical trial evaluating amlodipine for myocardial iron overload in thalassemia has completed.
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CLINICAL_TRIALS trial_result · 2017-06-14Clinical Trial Update: The Effective and Safety of Thalidomide in TI [Phase 2]
A Phase 2 clinical trial is investigating the efficacy and safety of thalidomide in the treatment of thalassemia; the current status is list…
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CLINICAL_TRIALS trial_result · 2017-05-25Clinical Trial Update: Use of Mobile Technology for Intensive Training in Medication Management [NA]
This clinical trial update notes a completed Duke University study evaluating the use of mobile technology to provide intensive training in …
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CLINICAL_TRIALS trial_result · 2017-05-09Clinical Trial Update: Stem Cell Transplant for Hemoglobinopathy [Phase 2, Phase 3]
Phase 2/3 trial update on stem cell transplant for hemoglobinopathy shows completed status with results posted.
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CLINICAL_TRIALS trial_result · 2017-03-22Clinical Trial Update: The Effective and Safety of Thalidomide in NTDT [Phase 2]
Trial update on the effectiveness and safety of thalidomide in non-transfusion-dependent thalassemia (Phase 2).
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CLINICAL_TRIALS trial_result · 2016-12-12Clinical Trial Update: This Study Will Evaluate Efficacy and Safety of Deferasirox in Patients With Myelodysplastic Syndromes (MDS), Thalassemia and Rare Anemia Types Having Transfusion-induced Iron Overload. [Phase 4]
Phase 4 trial by Novartis evaluated the efficacy and safety of deferasirox in patients with myelodysplastic syndrome, thalassemia, and trans…
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CLINICAL_TRIALS trial_result · 2016-10-05Clinical Trial Update: Effects of Transfusion of Older Stored Red Cells [NA]
A terminated clinical trial evaluated the effects of transfusing older stored red blood cells in people with sickle cell disease or thalasse…
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CLINICAL_TRIALS trial_result · 2016-09-19Clinical Trial Update: An Epidemiological Study to Assess Iron Overload Using MRI in Patients With Transfusional Siderosis (TIMES Study) [Phase 4]
Phase 4 epidemiological study update evaluating MRI-based assessment of iron overload in patients with thalassemia (including NTDT), myelody…
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CLINICAL_TRIALS trial_result · 2016-08-18Clinical Trial Update: A Pilot Study of HSCT for Patients With High-risk Hemoglobinopathy Using a Nonmyeloablative Preparative Regimen [NA]
A pilot hematopoietic stem cell transplant study using a nonmyeloablative preparative regimen in patients with high-risk hemoglobinopathies,…