Tetrahydrobiopterin Deficiency

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CLINICAL_TRIALS trial_result · 2020-09-25
Clinical Trial Update: Safety and Efficacy Study of Phenoptin in Subjects With Hyperphenylalaninemia Due to BH4 Deficiency [Phase 2]
Phase 2 safety and efficacy study of Phenoptin in subjects with hyperphenylalaninemia due to tetrahydrobiopterin deficiency has completed wi…