Stxbp1-related Encephalopathy

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CLINICAL_TRIALS trial_result · 2025-10-01
Clinical Trial Update: A Clinical Trial of CAP-002 Gene Therapy in Pediatric Patients With Syntaxin-Binding Protein 1 (STXBP1) Encephalopathy [Phase 1, Phase 2]
A clinical trial update indicates that the CAP-002 gene therapy trial in pediatric STXBP1-related encephalopathy (a developmental and epilep…