Records containing: Spinal Muscular Atrophy 1
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CLINICAL_TRIALS study record update · 2025-11-21A Multicenter, Open, Dose-escalation Clinical Study Evaluating the Safety, Initial Efficacy, and Immunogenicity of SKG0201 Injection in Patients With Spinal Muscular Atrophy Type 1
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CLINICAL_TRIALS study record update · 2025-09-11Evaluation of Palliative and Supportive Care for Spinal Muscular Atrophy (SMA) Type 1 Patients
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CLINICAL_TRIALS study record update · 2025-04-25A Long Term Follow up Safety Study of Patients in the AVXS-101-CL-101 Gene Replacement Therapy Clinical Trial for Spinal Muscular Atrophy Type 1 Delivering AVXS 101
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CLINICAL_TRIALS study record update · 2019-05-10Phase I Gene Transfer Clinical Trial for Spinal Muscular Atrophy Type 1 Delivering AVXS-101