Sly Syndrome
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS trial_result · 2019-10-16Clinical Trial Update: Study of UX003 Recombinant Human Beta-Glucuronidase (rhGUS) Enzyme Replacement Treatment in Mucopolysaccharidosis Type 7, Sly Syndrome (MPS 7) Patients Less Than 5 Years of Age [Phase 2]
Phase 2 clinical trial evaluating UX003 rhGUS enzyme replacement for MPS VII (Sly Syndrome) in children under 5; study completed with result…
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CLINICAL_TRIALS trial_result · 2019-07-30Clinical Trial Update: A Study of UX003 Recombinant Human Beta-Glucuronidase (rhGUS) Enzyme Replacement Therapy in Subjects With Mucopolysaccharidosis Type 7, Sly Syndrome (MPS 7) [Phase 3]
Phase 3 trial evaluating UX003 rhGUS for MPS VII (Sly syndrome) has completed; results posted in 2019.
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CLINICAL_TRIALS trial_result · 2018-02-19Clinical Trial Update: A Phase 3 Study of UX003 Recombinant Human Betaglucuronidase (rhGUS) Enzyme Replacement Therapy in Patients With Mucopolysaccharidosis Type 7 (MPS 7) [Phase 3]
Phase 3 study of UX003 rhGUS enzyme replacement therapy for MPS type 7 (Sly syndrome) completed with results posted in 2018.