Slc6a1-related Neurodevelopmental Disorder

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CLINICAL_TRIALS trial_result · 2025-09-15
Clinical Trial Update: Gene Therapy for SLC6A1 Neurodevelopmental Disorder [Phase 1, Phase 2]
A clinical trial update shows a gene therapy program for SLC6A1-related neurodevelopmental disorder is in Phase 1/Phase 2 and enrolling by i…