Slc13a5 Citrate Transporter Disorder
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CLINICAL_TRIALS trial_result · 2025-08-14Clinical Trial Update: Intrathecal Gene Therapy For SLC13A5 Citrate Transporter Disorder [Phase 1, Phase 2]
Phase 1/2 intrathecal gene therapy trial for SLC13A5 Citrate Transporter Disorder, currently NOT_YET_RECRUITING.