Records containing: SLC13A5 Citrate Transporter Disorder

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CLINICAL_TRIALS study record update · 2025-08-14
A Phase 1/2 Open-Label Intrathecal Administration of TSHA-105 to Determine the Safety and Efficacy in 2 Subjects With SLC13A5 Citrate Transporter Disorder Caused by a Mutation in the SLC13A5 Gene