Records containing: Sickle Cell Disease
This is the wording recorded or indexed by the source. An agency index term is not necessarily an authorised indication. Co-listed drug names are not linked to this term as a treatment relationship.
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CLINICAL_TRIALS study record update · 2026-03-09A Phase 3 Study to Evaluate the Safety and Efficacy of a Single Dose of CTX001 in Pediatric Subjects With Severe Sickle Cell Disease
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CLINICAL_TRIALS study record update · 2026-03-05Pilot Study to Evaluate the Safety and Feasibility of Induction of Mixed Chimerism in Sickle Cell Disease Patients With COH-MC-17: a Non-Myeloablative, Conditioning Regimen and CD4+ T-cell-depleted Haploidentical Hematopoietic Transplant
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CLINICAL_TRIALS study record update · 2026-03-05A Phase 1/2 Open Label Study Evaluating the Safety and Efficacy of Gene Therapy of the Sickle Cell Disease by Transplantation of an Autologous CD34+ Enriched Cell Fraction That Contains CD34+ Cells Transduced ex Vivo With the GLOBE1 Lentiviral Vector Expressing the βAS3 Globin Gene (GLOBE1 βAS3 Modified Autologous CD34+ Cells) in Patients With Sickle Cell Disease (SCD)
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CLINICAL_TRIALS study record update · 2026-03-05Primary Prevention of Stroke in Children With SCD in Sub-Saharan Africa II: A Multicenter, Open-label, Single-arm Type I Hybrid Clinical Trial
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CLINICAL_TRIALS study record update · 2026-03-05A Comparative Observational Study to Evaluate the Safety and Effectiveness of Xromi (Hydroxycarbamide Oral Solution 100mg/ml) for the Prevention of Vaso-occlusive Complications of Sickle Cell Disease in Children Under 2 Years of Age.
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CLINICAL_TRIALS study record update · 2026-03-04Sickle Cell Disease and CardiovAscular Risk - Red Cell Exchange Trial (SCD-CARRE)
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CLINICAL_TRIALS study record update · 2026-03-04A Phase 1/2 Open Label Cohort Study Evaluating the Efficacy and Safety of Gene Therapy of the Sickle Cell Disease (SCD) by Transplantation of an Autologous CD34+ Enriched Cell Fraction That Contains Autologous CD34+ Cells Transduced ex Vivo by the Bifunctional βAS3m/miR7m Lentiviral Vector Expressing the Therapeutical Beta-globin βAS3m and a Micro-RNA (miRNA) Targeting Specifically the Endogenous βS-globin mRNA.
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CLINICAL_TRIALS study record update · 2026-03-03Hybrid Effectiveness-Implementation Trial of Guided Relaxation and Acupuncture for Chronic Sickle Cell Disease Pain
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CLINICAL_TRIALS study record update · 2026-03-02The SickleFit Exercise and Nutrition Randomized Control Trial for Older Adults With Sickle Cell Disease
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CLINICAL_TRIALS study record update · 2026-02-27RCT of Stress Management and Mindfulness Intervention for Patients With Sickle Cell Disease
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CLINICAL_TRIALS study record update · 2026-02-27Safety and Efficacy of KL003 Cell Injection in Severe Sickle Cell Disease
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CLINICAL_TRIALS study record update · 2026-02-27The Cognitive-Remediation of Executive and Adaptive Deficits in Youth (C-READY) Intervention: A Randomized Controlled Trial for Adolescents With Sickle Cell Disease to Prepare for Transition of Care
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CLINICAL_TRIALS study record update · 2026-02-24Determination of Red Cell Survival in Sickle Cell Disease and Other Hemoglobinopathies Using Biotin Labeling
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CLINICAL_TRIALS study record update · 2026-02-23Writing Relaxing Beats in Adolescents Who Have Sickle Cell Disease
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CLINICAL_TRIALS study record update · 2026-02-20Phase 2a, Multicenter, Randomized, Double-blind, Placebo-controlled Study to Assess the Safety of Anumigilimab (CSL324) in Adults With Sickle Cell Disease
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CLINICAL_TRIALS study record update · 2026-02-18A Compassionate Release Protocol: Expanded Access to CD34+ Selection Utilizing Miltenyi CliniMACS Prodigy® for Patients Receiving Peripheral Blood Stem Cell Transplantations and Stem Cell Boosts
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CLINICAL_TRIALS study record update · 2026-02-18Prophylactic Transfusion In Pregnant in Women With Sickle Cell Disease
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CLINICAL_TRIALS study record update · 2026-02-13Mindfulness-Based Intervention for Pain and Sleep in Adolescents and Young Adults With Sickle Cell Disease
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CLINICAL_TRIALS study record update · 2026-02-13The Epidemiology of Silent and Overt Strokes in Adults With Sickle Cell Disease: a Prospective Cohort Study
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CLINICAL_TRIALS study record update · 2026-02-12A Phase 1 Open-Label, Multiple-Dose Study to Evaluate Safety and Tolerability, Pharmacokinetics and Pharmacodynamics of FTX-6058 in Subjects With Sickle Cell Disease (SCD)
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CLINICAL_TRIALS study record update · 2026-02-10An Open-Label Study to Evaluate the Safety and Efficacy of a Single Dose of Autologous CD34+ Human Hematopoietic Stem Cells Modified Using Transformer Base Editor in Participants With Severe Sickle Cell Disease
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CLINICAL_TRIALS study record update · 2026-02-09Early Life Exposures Among Children With Sickle Cell Disease
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CLINICAL_TRIALS study record update · 2026-02-06Longitudinal Examination of Predictors and Outcomes of Sickle Cell Disease Healthcare Transition
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CLINICAL_TRIALS study record update · 2026-02-05Multicenter Observational Study on Myocardial Iron Overload in 3 Multitransfused Populations
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CLINICAL_TRIALS study record update · 2026-02-05A Phase I Study to Evaluate the Safety and Tolerability of Escalating Doses of Fostamatinib in Subjects With Stable Sickle Cell Disease