Clinical Trial Update: Evaluation of Safety and Efficacy of CTX001 in Pediatric Participants With Severe Sickle Cell Disease (SCD) [Phase 3]

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Summary

Phase 3 clinical trial update on the safety and efficacy of CTX001 in pediatric patients with severe sickle cell disease; the study is currently active but not …

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Diseases / indications

• Sickle Cell Disease

Drugs mentioned

• CTX001

Snippet

Sponsor: Vertex Pharmaceuticals Incorporated | Conditions: Sickle Cell Disease, Hydroxyurea Failure | Phase 3 | Status: ACTIVE_NOT_RECRUITING