Sickle Cell-beta-thalassemia
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CLINICAL_TRIALS research · 2026-04-24Clinical Trial Update: Investigating the Mechanistic Effects of Mitapivat in Subjects With Sickle Cell Disease
This clinical trial update describes investigations into the mechanistic effects of mitapivat in subjects with sickle cell disease, which is…
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CLINICAL_TRIALS research · 2025-08-14Clinical Trial Update: CD34+ (Non-Malignant) Stem Cell Selection for Patients Receiving Allogeneic Stem Cell Transplantation [Phase 1, Phase 2]
This document provides an update on a phase 1/2 clinical trial evaluating CD34+ stem cell selection for patients receiving allogeneic stem c…
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CLINICAL_TRIALS trial_result · 2024-10-28Clinical Trial Update: Pharmacokinetics of Oral Hydroxyurea Solution [Phase 1, Phase 2]
Completed Phase 1/2 pharmacokinetics study of an oral hydroxyurea solution in sickle cell disease and related hemoglobin disorders, with res…