Combined Immunodeficiency Due to Ada Deficiency
📧 Sign up to get email alerts when something new happens for Combined Immunodeficiency Due to Ada Deficiency.
Sign up freeTop drugs studied for this disease
-
CLINICAL_TRIALS trial_result · 2023-02-01Clinical Trial Update: Efficacy and Safety of the Cryopreserved Formulation of OTL-101 in Subjects With ADA-SCID [Phase 1, Phase 2]
A clinical trial update reports on the efficacy and safety of a cryopreserved formulation of OTL-101 in subjects with ADA-SCID, spanning Pha…
-
CLINICAL_TRIALS withdrawal · 2022-08-03Clinical Trial Update: A Clinical Study to Enable Process Validation of Commercial Grade OTL-101 [Phase 2, Phase 3]
A clinical study aimed at enabling process validation for OTL-101 has been withdrawn after Phase 2/3 was in progress.
-
CLINICAL_TRIALS trial_result · 2022-07-22Clinical Trial Update: Efficacy and Safety of the Cryopreserved Formulation of OTL-101 in Subjects With ADA-SCID [Phase 1, Phase 2]
Phase 1/2 trial update on the cryopreserved formulation of OTL-101 for ADA-SCID assessing efficacy and safety.