Selenoprotein N-related Myopathy

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CLINICAL_TRIALS trial_result · 2020-09-29
Clinical Trial Update: Pharmacological Treatment of a Rare Genetic Disease: N-acetylcysteine in Myopathy Associated Selenoprotein N-related Myopathy (SEPN1-RM) [Phase 2, Phase 3]
Phase 2/3 clinical trial evaluating N-acetylcysteine for Selenoprotein N-related Myopathy (SEPN1-RM) has been terminated.