Sandhoff Disease

Top drugs studied for this disease

All Approvals Safety alerts Label changes Trial results Research Guidance Withdrawals

CLINICAL_TRIALS withdrawal · 2013-02-25
Clinical Trial Update: A Phase I Study of Pyrimethamine in Patients With GM2 Gangliosidosis [Phase 1]
A Phase I clinical trial of pyrimethamine for GM2 gangliosidosis (including Tay-Sachs and Sandhoff diseases) has been withdrawn.