Rpe65-related Retinal Dystrophy
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CLINICAL_TRIALS research · 2025-09-22Clinical Trial Update: A Patient Registry Study for Patients Treated With Voretigene Neparvovec in US
This clinical trial registry entry reports a completed U.S. patient registry study of Voretigene Neparvovec (Luxturna) for biallelic RPE65 m…
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CLINICAL_TRIALS research · 2025-04-25Clinical Trial Update: Study of Efficacy and Safety of Voretigene Neparvovec in Japanese Patients With Biallelic RPE65 Mutation-associated Retinal Dystrophy [Phase 3]
Phase 3 study evaluating efficacy and safety of voretigene neparvovec in Japanese patients with biallelic RPE65 mutation-associated retinal …