Retinal Dystrophy
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS research · 2026-04-20Clinical Trial Update: Oral Metformin for Treatment of ABCA4 Retinopathy [Phase 1, Phase 2]
An oral metformin trial for ABCA4 retinopathy and Stargardt disease is in Phase 1/Phase 2 and currently recruiting.
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CLINICAL_TRIALS research · 2026-04-14Clinical Trial Update: Real-time Acoustic Biofeedback for Enhancing Fixation Stability: A Proof-of-concept Study to Improve Ophthalmic Imaging Diagnostic Quality [NA]
A proof-of-concept clinical trial evaluating real-time acoustic biofeedback to stabilize fixation and improve ophthalmic imaging quality in …
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CLINICAL_TRIALS research · 2025-10-06Clinical Trial Update: SS-HH-OCT as a Novel Diagnostic Modality for Early-Onset Retinal Dystrophies (EORDs) [NA]
Clinical trial evaluating SS-HH-OCT as a novel diagnostic modality for early-onset retinal dystrophy conditions; study currently recruiting …
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CLINICAL_TRIALS research · 2025-09-16Clinical Trial Update: Personalized Antisense Oligonucleotide Therapy for a Single Participant With PRPH2 Mutation Associated With Retinal Dystrophy [Phase 1, Phase 2]
A clinical trial update describes a personalized antisense oligonucleotide therapy studied in a single participant with a PRPH2 mutation cau…
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CLINICAL_TRIALS research · 2025-04-03Clinical Trial Update: Functional Assessments in Vision Impairment
A clinical trial update from the Center for Eye Research Australia describes a study evaluating functional assessments in vision impairment …
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CLINICAL_TRIALS research · 2025-01-08Clinical Trial Update: Observational Study to Assess Endpoint Operational Feasibility & Measurement Properties in Patients with Retinal Degeneration
This clinical trial update describes an observational study to assess endpoint feasibility and measurement properties in patients with retin…
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CLINICAL_TRIALS research · 2011-11-24Clinical Trial Update: Genetic Study of Patients Suffering From Congenital Amaurosis of Leber or From an Early Severe Retinal Dystrophy [NA]
A completed genetic study investigating patients with Leber congenital amaurosis and early severe retinal dystrophy.