Pyruvate Dehydrogenase Deficiency

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CLINICAL_TRIALS research · 2026-03-31
Clinical Trial Update: Efficacy and Safety of the Treatment of Pyruvate Dehydrogenase Deficiency Patients With Glycerol Phenylbutyrate (RAVICTI) [Phase 2]
Phase 2 trial evaluating the efficacy and safety of glycerol phenylbutyrate (RAVICTI) in patients with Pyruvate Dehydrogenase Deficiency; cu…