Records containing: Pyruvate Dehydrogenase Complex Deficiency Disease
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CLINICAL_TRIALS study record update · 2026-03-31A Phase II, Multicentric, Prospective, Non-comparative Clinical Trial to Assess the Efficacy and Safety of the Treatment of Pyruvate Dehydrogenase Deficiency (PDH) Patients With Glycerol Phenybutyrate (RAVICTI®)
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CLINICAL_TRIALS study record update · 2026-02-13Natural History and Advanced Genetic Study of Pyruvate Dehydrogenase Complex Deficiencies (North American Mitochondrial Disease Consortium, Rare Diseases Clinical Research Network, Project 7413)
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CLINICAL_TRIALS study record update · 2025-05-29Coordination of Rare Diseases at Sanford