Progressive Myoclonus Epilepsy
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CLINICAL_TRIALS research · 2026-03-18Clinical Trial Update: Registry and Natural History Study for Progressive Myoclonus Epilepsy Type 1 (EPM1)
This registry entry describes a natural history study for Progressive Myoclonus Epilepsy Type 1 (EPM1) at Boston Children's Hospital, which …
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CLINICAL_TRIALS trial_result · 2025-03-25Clinical Trial Update: Safety, Blood Levels and Effects of AUT00201 in Patients With MEAK [Phase 1]
Phase 1 trial assessing safety, blood levels, and exploratory effects of AUT00201 in patients with progressive myoclonus epilepsy; results c…