Records containing: Primary Hyperoxaluria Type 1

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CLINICAL_TRIALS study record update · 2026-04-24
BONAPH1DE, A Prospective Observational Study of Patients With Primary Hyperoxaluria Type 1 (PH1)
CLINICAL_TRIALS study record update · 2026-04-16
A Phase 2 Open-Label Multicenter Study to Evaluate the Safety, Pharmacokinetics, and Efficacy of Nedosiran in Pediatric Patients From Birth to 11Years of Age With Primary Hyperoxaluria and Relatively Intact Renal Function
CLINICAL_TRIALS study record update · 2025-12-24
A Phase 2 Open-Label Study to Evaluate the Safety and Efficacy of DCR-PHXC in Patients With Primary Hyperoxaluria Type 1 and Severe Renal Impairment, With or Without Dialysis
CLINICAL_TRIALS study record update · 2025-04-04
Early Check: A Collaborative Innovation to Facilitate Pre-Symptomatic Clinical Trials in Newborns
CLINICAL_TRIALS study record update · 2024-07-11
A Phase 1 Study of DCR-PH1 in Patients With Primary Hyperoxaluria Type 1 (PH1)
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CLINICAL_TRIALS study record update · 2024-06-18
Evaluation of the Efficacy and Safety of Stiripentol in Patients 6 Years and Older With Primary Hyperoxaluria Type 1, 2 or 3
CLINICAL_TRIALS study record update · 2022-07-12
ILLUMINATE-C: A Single Arm Study to Evaluate Efficacy, Safety, Pharmacokinetics, and Pharmacodynamics of Lumasiran in Patients With Advanced Primary Hyperoxaluria Type 1 (PH1)
CLINICAL_TRIALS study record update · 2019-06-12
"Pilot Study: Proteomics of Primary Hyperoxaluria Type 1 (PH1): A Rare Calcium Oxalate Stone Disease"
CLINICAL_TRIALS study record update · 2016-07-13
ClinicalTrials.gov study NCT02830009