Prader-willi Syndrome
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Sign up freeTop drugs studied for this disease
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CLINICAL_TRIALS research · 2026-04-24Clinical Trial Update: Impact of Bright Light Therapy on Prader-Willi Syndrome [NA]
A clinical trial is evaluating the impact of bright light therapy on Prader-Willi Syndrome, with recruitment currently ongoing.
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CLINICAL_TRIALS research · 2026-04-16Clinical Trial Update: Observational Study of VYKAT™ XR in Patients With Prader-Willi Syndrome
An observational study evaluating VYKAT XR in patients with Prader-Willi Syndrome, sponsored by Soleno Therapeutics, Inc., currently enrolli…
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CLINICAL_TRIALS trial_result · 2026-04-09Clinical Trial Update: ARD-101 for Treatment of PWS: The Hunger Elimination or Reduction Objective Trial [Phase 3]
Phase 3 trial ARD-101 for Prader-Willi syndrome-related hyperphagia has been suspended.
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CLINICAL_TRIALS other · 2026-04-08Clinical Trial Update: PWS European Blood Bank for Infants and Controls From 0 to 48 Months [NA]
This clinical trial update notes that the Prader-Willi Syndrome study involving infants and controls from birth to 48 months has completed.
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CLINICAL_TRIALS trial_result · 2026-04-06Clinical Trial Update: A Clinical Evaluation of Non-Invasive Vagus Nerve Stimulation for Temper Outbursts in People With PWS [Phase 3]
This is a Phase 3 clinical trial evaluating non-invasive vagus nerve stimulation to reduce temper outbursts in people with Prader-Willi Synd…
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CLINICAL_TRIALS research · 2026-03-27Clinical Trial Update: The Intervention of Obesity in Children With Prader-Willi Syndrome Using Prebiotics and Probiotics [NA]
A clinical trial investigates whether prebiotics and probiotics can help manage obesity in children with Prader-Willi syndrome. The study is…
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CLINICAL_TRIALS other · 2026-03-19Clinical Trial Update: The Hunger Elimination or Reduction Objective (HERO ) Open -Label Extension (OLE) Trial [Phase 3]
The Phase 3 HERO open-label extension trial for Prader-Willi syndrome-related hyperphagia has been suspended.
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CLINICAL_TRIALS research · 2026-03-17Clinical Trial Update: A Study of Pitolisant in Participants With Prader-Willi Syndrome [Phase 3]
Phase 3 clinical trial evaluating pitolisant for Prader-Willi syndrome is currently enrolling by invitation.
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CLINICAL_TRIALS research · 2026-03-17Clinical Trial Update: A Study of Pitolisant in Patients With Prader-Willi Syndrome [Phase 3]
Harmony Biosciences is conducting a Phase 3 trial to evaluate pitolisant for Prader-Willi Syndrome, and recruitment is ongoing.
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CLINICAL_TRIALS research · 2026-02-23Clinical Trial Update: Physical Activity and Community EmPOWERment Project [NA]
Clinical trial update from the University of North Carolina on the Physical Activity and Community Empowerment project. The study is current…
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CLINICAL_TRIALS research · 2026-02-12Clinical Trial Update: A Study of Setmelanotide in Patients With Prader-Willi Syndrome [Phase 2]
This is an update on a Phase 2 trial of setmelanotide for Prader-Willi syndrome, with obesity and hyperphagia as related conditions. The stu…
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CLINICAL_TRIALS research · 2026-02-12Clinical Trial Update: IDMet (RaDiCo Cohort) (RaDiCo-IDMet)
The RaDiCo-IDMet cohort study sponsored by INSERM is enrolling participants to study imprinting-related disorders including Silver-Russell s…
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CLINICAL_TRIALS research · 2026-01-16Clinical Trial Update: A Study of CSTI-500 in Patients With Prader-Willi Syndrome [Phase 2]
A Phase 2 clinical trial of CSTI-500 for Prader-Willi syndrome is announced, though it is not yet recruiting. The sponsor listed is ConSynan…
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CLINICAL_TRIALS research · 2025-12-22Clinical Trial Update: A Study of RM-718 in Healthy Subjects and Patients With MC4R Pathway Impairment [Phase 1, Phase 2]
A Clinical Trial Update indicates RM-718 is being studied in Phase 1/Phase 2 in healthy subjects and patients with MC4R pathway impairment, …
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CLINICAL_TRIALS research · 2025-12-05Clinical Trial Update: A 2-Part Study to Assess Efficacy, Safety and Tolerability of BMB-101 for the Treatment of Patients With Prader-Willi Syndrome. [Phase 2]
This clinical trial update describes a Phase 2 study evaluating the efficacy, safety, and tolerability of BMB-101 for Prader-Willi Syndrome,…
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CLINICAL_TRIALS trial_result · 2025-12-05Clinical Trial Update: Effects of Intranasal Administration of Oxytocin in Adults With Prader-Willi Syndrome [Phase 2, Phase 3]
An update on a Phase 2/3 trial evaluating intranasal oxytocin in adults with Prader-Willi syndrome. The study status is completed.
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CLINICAL_TRIALS research · 2025-12-05Clinical Trial Update: Cerebellar TMS and Satiety in Prader-Willi Syndrome [NA]
A Brigham and Women’s Hospital-sponsored clinical trial is evaluating cerebellar transcranial magnetic stimulation to influence satiety in P…
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CLINICAL_TRIALS research · 2025-12-03Clinical Trial Update: OLE Study of Carbetocin Nasal Spray for the Treatment of Hyperphagia in Prader-Willi Syndrome [Phase 3]
ACADIA Pharmaceuticals is conducting an ongoing Phase 3 open-label extension study of carbetocin nasal spray to treat hyperphagia in Prader-…
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CLINICAL_TRIALS trial_result · 2025-10-22Clinical Trial Update: A Phase 2 Study to Evaluate the Safety and Efficacy of Pitolisant in Patients With Prader-Willi Syndrome, Followed by an Open Label Extension [Phase 2]
Phase 2 trial results evaluate the safety and efficacy of pitolisant in Prader-Willi Syndrome, with an open-label extension.
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CLINICAL_TRIALS trial_result · 2025-10-03Clinical Trial Update: Improving Care of Prader-Willi Syndrome : Evaluation of a New Care Program Combining Adapted Physical Activity, Nutrition and Therapeutic Education [NA]
A completed clinical trial evaluating a care program that combines adapted physical activity, nutrition, and therapeutic education for peopl…
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CLINICAL_TRIALS research · 2025-09-16Clinical Trial Update: Tirzepatide in PWS, HO and GNSO [Phase 4]
Phase 4 clinical trial evaluating tirzepatide for Prader-Willi Syndrome and hypothalamic obesity is currently recruiting.
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CLINICAL_TRIALS trial_result · 2025-09-10Clinical Trial Update: Study of Carbetocin Nasal Spray for the Treatment of Hyperphagia in Prader-Willi Syndrome [Phase 3]
A Phase 3 clinical trial of carbetocin nasal spray for hyperphagia in Prader-Willi syndrome is currently active but not recruiting.
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EMA approval · 2025-08-05EMA Authorised: Omnitrope (somatropin) — Sandoz GmbH
The European Medicines Agency authorised Omnitrope (somatropin) by Sandoz GmbH for the treatment of Turner syndrome, Prader-Willi syndrome, …
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CLINICAL_TRIALS research · 2025-07-31Clinical Trial Update: Parent and Infant Inter(X)Action Intervention (PIXI) [NA]
Clinical trial update for the PIXI Inter(X)Action Intervention (NCT03836300), currently enrolling by invitation across Fragile X Syndrome, A…
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FDA approval · 2025-07-09FDA Approved: OMNITROPE — Supplemental Application (Sandoz Inc)
FDA approved a supplemental application for OMNITROPE (somatropin) submitted by Sandoz Inc.