Posterior Column Ataxia with Retinitis Pigmentosa
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CLINICAL_TRIALS research · 2025-01-27Clinical Trial Update: Antisense Oligonucleotide Treatment for PCARP Disease Due to Mutation in FLVCR1 [EARLY_Phase 1]
An antisense oligonucleotide therapy for FLVCR1-related Posterior Column Ataxia with Retinitis Pigmentosa is in EARLY_PHASE1 and currently e…