Records containing: Pompe's Disease
This is the wording recorded or indexed by the source. An agency index term is not necessarily an authorised indication. Co-listed drug names are not linked to this term as a treatment relationship.
Follow recorded terms in Drug Alerts for Android. Free includes unlimited local condition follows and an on-open recent-record watchlist. Plus adds no ads and personal organization tools.
All
FDA submission records
EMA medicine records
ClinicalTrials.gov record updates
ClinicalTrials.gov records with results posted
-
CLINICAL_TRIALS study record update · 2026-03-23A Single-arm, Open-label, Phase 4 Study to Evaluate the Safety and Efficacy of Avalglucosidase Alfa in Chinese Participants With Infantile-onset Pompe Disease (IOPD)
-
CLINICAL_TRIALS study record update · 2025-02-10A Single Arm, Prospective, Open-label, Multi-center Study to Evaluate Efficacy and Safety in Chinese Patients With Late Onset Pompe Disease With Alglucosidase Alfa Treatment
-
CLINICAL_TRIALS study record update · 2016-09-19Feasability and Interest of Screening for Infantile Pompe's Diseases at Birth
-
CLINICAL_TRIALS study record update · 2016-09-16Prevalence of Heterozygote Mothers for Pompe's Disease Among Mothers Having Delivered in French Guiana
-
CLINICAL_TRIALS study record update · 2015-08-18Prevalence of Pompe's Disease Amongst Patients With Unexplained Respiratory Muscle Weakness or Respiratory Failure
- Organize your saved records without ads with Plus.
-
CLINICAL_TRIALS study record update · 2011-12-08Pompe Prevalence Study in Patients With Muscle Weakness Without Diagnosis