Pompe Disease
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CLINICAL_TRIALS trial_result · 2013-01-01Clinical Trial Update: Newborn Screening Assay of Pompe's Disease [NA]
The document reports the completion of a clinical trial evaluating a newborn screening assay for Pompe disease conducted by National Taiwan …
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CLINICAL_TRIALS trial_result · 2012-03-16Clinical Trial Update: 3D Echocardiography Managing Infantile Pompe's Disease
An update indicates that the clinical trial evaluating 3D echocardiography for managing infantile Pompe disease has been terminated.
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CLINICAL_TRIALS trial_result · 2012-01-05Clinical Trial Update: Late-Onset Treatment Study Extension Protocol [Phase 4]
Phase 4 study extension for late-onset Pompe disease and glycogen storage disease type II; the trial is completed and results were posted in…
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CLINICAL_TRIALS trial_result · 2011-04-22Clinical Trial Update: High Dose or High Dose Frequency Study of Alglucosidase Alfa [Phase 4]
Phase 4 clinical trial evaluating high-dose or high-dose-frequency alglucosidase alfa in Pompe disease completed with results posted in 2011…
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CLINICAL_TRIALS trial_result · 2010-07-23Clinical Trial Update: A Placebo-Controlled Study of Safety and Effectiveness of Myozyme (Alglucosidase Alfa) in Patients With Late-Onset Pompe Disease [Phase 3]
A Phase 3, placebo-controlled trial evaluating the safety and efficacy of Myozyme (alglucosidase alfa) in late-onset Pompe disease has compl…
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